Duchenne muscular dystrophy is a complex condition affecting many parts of the body; as a result approaches to treating the condition can focus on many different areas including correcting the Dystrophin gene, reducing inflammation or protecting the heart.
We have listed the potential therapies below, with more detailed pages you can click through.
Contact us on 07535 498 506 if you would like to discuss the science behind Duchenne and how potential treatment could help your family.
- Muscle and Cell Biology Basics
- Anti-fibrotics
- Anti-inflammatory Drugs
- Calcium/Sodium Exchanger
- Cardiomyopathy
- Exon Skipping
- Gene Editing (CRISPR/CAS9)
- Gene Therapy
- Mitochondria
- Multimodal Pathways
- Muscle Cellular Stress
- NF-kB Inhibitor
- Other Protein Targets
- Rare Repurposing in Duchenne
- Stem Cell Therapy
- Stop Codon Readthrough
- Testosterone
